256. 筋型糖原病 Muscle glycogenosis Clinical trials / Disease details

臨床試験数 : 180 / 薬物数 : 153 - (DrugBank : 30) / 標的遺伝子数 : 31 - 標的パスウェイ数 : 134

1 trial found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03533673 (ClinicalTrials.gov)	November 1, 2018	13/4/2018	AAV2/8-LSPhGAA in Late-Onset Pompe Disease	A Phase 1 Study of the Safety of AAV2/8-LSPhGAA in Late-onset Pompe Disease	Pompe Disease	Biological: AAV2/8LSPhGAA	Asklepios Biopharmaceutical, Inc.	Duke University;National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)	Recruiting	18 Years	N/A	All	8	Phase 1/Phase 2	United States

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