256. 筋型糖原病 Muscle glycogenosis Clinical trials / Disease details
臨床試験数 : 180 / 薬物数 : 153 - (DrugBank : 30) / 標的遺伝子数 : 31 - 標的パスウェイ数 : 134
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT03533673 (ClinicalTrials.gov) | November 1, 2018 | 13/4/2018 | AAV2/8-LSPhGAA in Late-Onset Pompe Disease | A Phase 1 Study of the Safety of AAV2/8-LSPhGAA in Late-onset Pompe Disease | Pompe Disease | Biological: AAV2/8LSPhGAA | Asklepios Biopharmaceutical, Inc. | Duke University;National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) | Recruiting | 18 Years | N/A | All | 8 | Phase 1/Phase 2 | United States |