256. 筋型糖原病 Muscle glycogenosis Clinical trials / Disease details

臨床試験数 : 180 / 薬物数 : 153 - (DrugBank : 30) / 標的遺伝子数 : 31 - 標的パスウェイ数 : 134

2 trials found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT01885936 (ClinicalTrials.gov)	June 2013	21/6/2013	Safety and Efficacy of Albuterol in Individuals With Late-onset Pompe Disease	A Phase 1/2 Double-Blind Study of the Safety and Efficacy of Albuterol on Motor Function in Individuals With Late-onset Pompe Disease Receiving Enzyme Replacement Therapy	Pompe Disease	Drug: Albuterol;Drug: Placebo	Duke University	NULL	Completed	18 Years	N/A	All	16	Phase 1/Phase 2	United States
2	NCT01859624 (ClinicalTrials.gov)	June 2012	8/5/2013	Albuterol in Individuals With Late Onset Pompe Disease (LOPD)	A Clinical Investigation of the Safety and Efficacy of Albuterol on Motor Function in Individuals With Late-onset Pompe Disease, Whether or Not Receiving Enzyme Replacement Therapy	Pompe Disease	Drug: Albuterol	Duke University	NULL	Completed	18 Years	N/A	All	8	Phase 1	United States