DDrare
Disease
Drug
Target Gene/Pathway
問合せ先
EN
256. 筋型糖原病
Muscle glycogenosis
Clinical trials
/
Disease details
臨床試験数
:
180
/
薬物数
:
153
- (
DrugBank
:
30
) /
標的遺伝子数
:
31
-
標的パスウェイ数
:
134
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No.
TrialID
Date_
enrollment
Date_
registration
Public_title
Scientific_title
Condition
Intervention
Primary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
Phase
Countries
1
NCT02525172
(
ClinicalTrials.gov
)
August 2015
10/8/2015
Immune Modulation Therapy for Pompe Disease
Immune Modulation Therapy for ERT-naïve or ERT-treated Pompe Disease Patients
Pompe Disease
Drug:
Rituximab
;Drug:
intravenous immune globulin
;Drug:
Bortezomib
;Drug:
Methotrexate
National Taiwan University Hospital
NULL
Recruiting
N/A
N/A
Both
8
Phase 4
Taiwan