256. 筋型糖原病 Muscle glycogenosis Clinical trials / Disease details

臨床試験数 : 180 / 薬物数 : 153 - (DrugBank : 30) / 標的遺伝子数 : 31 - 標的パスウェイ数 : 134

2 trials found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT04094948 (ClinicalTrials.gov)	January 1, 2023	17/9/2019	Phase II Clinical Trial of Clenbuterol in Adult Patients With Pompe Disease	Phase II Clinical Trial of Clenbuterol in Adult Patients With Pompe Disease Stably Treated With Enzyme Replacement Therapy	Pompe Disease (Late-onset)	Drug: Clenbuterol;Drug: Placebos	Duke University	NULL	Not yet recruiting	18 Years	N/A	All	40	Phase 2	United States
2	NCT01942590 (ClinicalTrials.gov)	September 2013	11/9/2013	Safety and Efficacy of Clenbuterol in Individuals With Late-onset Pompe Disease and Receiving Enzyme Replacement Therapy	A Clinical Investigation of the Safety and Efficacy of Clenbuterol on Motor Function in Individuals With Late-onset Pompe Disease and Receiving Enzyme Replacement Therapy	Pompe Disease	Drug: Clenbuterol;Drug: Placebo	Dwight Koeberl, M.D., Ph.D.	NULL	Completed	18 Years	N/A	All	17	Phase 1/Phase 2	United States