256. 筋型糖原病 Muscle glycogenosis Clinical trials / Disease details
臨床試験数 : 180 / 薬物数 : 153 - (DrugBank : 30) / 標的遺伝子数 : 31 - 標的パスウェイ数 : 134
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT04476550 (ClinicalTrials.gov) | February 1, 2022 | 26/2/2020 | Clinical Specimen Collection From Pompe Disease Patients | Developing a Potential Cure for Pompe Disease: Clinical Specimen Collection From Individuals With Pompe Disease | Pompe Disease | Drug: Filgrastim | Serhat Gumrukcu, MD PhD | Frida Therapeutics LLC | Recruiting | 3 Years | 30 Years | All | 12 | United States |