3. 脊髄性筋萎縮症 Spinal muscular atrophy Clinical trials / Disease details

臨床試験数 : 217 / 薬物数 : 149 - (DrugBank : 33) / 標的遺伝子数 : 54 - 標的パスウェイ数 : 80

1 trial found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT01645787 (ClinicalTrials.gov)	June 2012	5/7/2012	Short and Long Term Treatment With 4-AP in Ambulatory SMA Patients	Columbia SMA Project: 4-AP as a Potential SMA Therapeutic Agent and Biological Mechanisms of Action	Spinal Muscular Atrophy	Drug: 4-aminopyridine;Drug: Placebo	Columbia University	NULL	Completed	18 Years	50 Years	Both	11	Phase 2/Phase 3	United States