307. カナバン病 Canavan disease Clinical trials / Disease details


臨床試験数 : 5 薬物数 : 9 - (DrugBank : 3) / 標的遺伝子数 : 2 - 標的パスウェイ数 : 2

  
2 trials found
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PhaseCountries
1NCT00657748
(ClinicalTrials.gov)
September 20099/4/2008Lithium and Acetate for Canavan DiseaseEvaluation of the Tolerance and Efficiency of a Combined Oral Therapy With Lithium and GTA in Patients With Canavan DiseaseCanavan Disease;Infantile;Deficiency Disease;Aspartoacylase;Leukodystrophy, SpongiformDrug: Lithium Gluconate (drug) Glyceryl Triacetate GTA (drug)Assistance Publique - Hôpitaux de ParisEuropean Leukodystrophy Association;European Leukodystrophy AssociationWithdrawn1 Year15 YearsBoth0Phase 2France
2NCT00724802
(ClinicalTrials.gov)
March 200818/6/2008Oral Glyceryl Triacetate (GTA) in Newborns With CanavanOral Glyceryl Triacetate (GTA) in Newborns With CanavanCanavan DiseaseDietary Supplement: GTA (Glyceryl triacetate);Drug: GTA glyceryl triacetateShaare Zedek Medical CenterNULLRecruitingN/A18 MonthsBoth1N/AIsrael