329. 無虹彩症 Aniridia Clinical trials / Disease details


臨床試験数 : 3 薬物数 : 2 - (DrugBank : 2) / 標的遺伝子数 : 0 - 標的パスウェイ数 : 0

  
2 trials found
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT04117880
(ClinicalTrials.gov)
December 31, 201819/9/2019A Phase 2 Open Label Extension Study in Participants With Nonsense Mutation AniridiaNonsense Mutation Aniridia: An Ataluren (PTC124) Phase 2 Extension StudyAniridiaDrug: AtalurenPTC TherapeuticsNULLWithdrawn2 YearsN/AAll0Phase 2NULL
2NCT02647359
(ClinicalTrials.gov)
January 31, 201629/12/2015Study of Ataluren in Participants With Nonsense Mutation AniridiaSTAR: A Phase 2, Multicenter, Randomized, Double-Masked, Placebo-Controlled Study of the Safety and Efficacy of Ataluren (PTC124) for the Treatment of Nonsense Mutation AniridiaAniridiaDrug: Ataluren;Drug: PlaceboPTC TherapeuticsNULLCompleted2 YearsN/AAll39Phase 2United States;Canada