Long-term safety and tolerability of iptacopan in patients with Paroxysmal Nocturnal Hemoglobinuria
An open label, multicenter roll-over extension program (REP) to characterize the long-term safety and tolerability of iptacopan (LNP023) in patients with Paroxysmal Nocturnal Hemoglobinuria (PNH) who have completed PNH Phase 2 and Phase 3 studies with iptacopan. - - An open label, multicenter roll-over extension program (REP) to characterize the long-term safety an ...