DDrare
Disease
Drug
Target Gene/Pathway
問合せ先
EN
65. 原発性免疫不全症候群
Primary immunodeficiency
Clinical trials
/
Disease details
臨床試験数
:
482
/
薬物数
:
653
- (
DrugBank
:
119
) /
標的遺伝子数
:
92
-
標的パスウェイ数
:
212
Search
1 trial found
10
50
100
ALL
diseases per page:
Showing 1 to 1 of 1 diseases
Filter by
Reset
No.
TrialID
Date_
enrollment
Date_
registration
Public_title
Scientific_title
Condition
Intervention
Primary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
Phase
Countries
1
EUCTR2009-017346-32-IT
(
EUCTR
)
15/03/2010
26/04/2010
HAEMATOPOIETIC STEM CELL GENE THERAPY
A PHASE I/II CLINICAL TRIAL OF HAEMATOPOIETIC STEM CELL GENE THERAPY FOR THE WISKOTT-ALDRICH SYNDROME - TIGET-WAS
A PHASE I/II CLINICAL TRIAL OF HAEMATOPOIETIC STEM CELL GENE THERAPY FOR THE WISKOTT-ALDRICH SYNDROM ...
Wiskott-Aldrich Syndrom
MedDRA version: 20.0;Level: PT;Classification code 10061598;Term: Immunodeficiency;System Organ Class: 10021428 - Immune system disorders;Therapeutic area: Diseases [C] - Immune System Diseases [C20]
Wiskott-Aldrich Syndrom
MedDRA version: 20.0;Level: PT;Classification code 10061598;Term: Immunodefi ...
Trade Name:
FLUDARABINA
TEVA - 25 MG/ML CONCENTRATO PER SOLUZIONE INIETTABILE O PER INFUSIONE 1 FLACONCINO DI VETRO DA 2 ML
Product Name: na
Product Code: [na]
INN or Proposed INN:
FLUDARABINA
Other descriptive name:
FLUDARABINA
Trade Name:
MOZOBIL
- 20 MG/ML - SOLUZIONE INIETTABILE - USO SOTTOCUTANEO - FLACONCINO (VETRO) - 24 MG/1.2 ML 1 FLACONCINO
Product Name:
PLERIXAFOR
Product Code: [na]
INN or Proposed INN:
PLERIXAFOR
Other descriptive name:
Plerixafor
Trade Name:
MYELOSTIM - 34 1 FLACONCINO LIOFILIZZATO 33.6 MIU + SIRINGA PRERIEMPITA SOLVENTE 1 ML
Product Name: na
Product Code: [na]
INN or Proposed INN:
LENOGRASTIM
Trade Name:
MABTHERA
- 2 FIALE 100 MG 10 ML
Product Name:
RITUXIMAB
Product Code: [na]
INN or Proposed INN:
RITUXIMAB
Other descriptive name:
RITUXIMAB
Trade Name:
BUSILVEX
- 6 MG/ML - CONCENTRATO PER SOLUZIONE PER INFUSIONE - USO ENDOVENOSO - FLACONCINO - 10 ML 8 FLACONCINI
Product Name: na
Product Code: [na]
Trade Name:
FLUDARABINA
TEVA - 25 MG/ML CONCENTRATO PER SOLUZIONE INIETTABILE O PER INFUSIONE 1 FLACO
...
Orchard Therapeutics (Europe) Ltd
NULL
Authorised-recruitment may be ongoing or finished
Female: no
Male: yes
8
Phase 1;Phase 2
Italy