AVI-4658 (PMO) ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
113筋ジストロフィー1

113. 筋ジストロフィー


臨床試験数 : 622 薬物数 : 485 - (DrugBank : 99) / 標的遺伝子数 : 59 - 標的パスウェイ数 : 168
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT00159250
(ClinicalTrials.gov)
October 26, 20078/9/2005Safety and Efficacy Study of Antisense Oligonucleotides in Duchenne Muscular DystrophyRestoring Dystrophin Expression in Duchenne Muscular Dystrophy: A Phase I/II Clinical Trial Using AVI-4658Duchenne Muscular DystrophyDrug: AVI-4658 (PMO)Imperial College LondonDepartment of Health, United Kingdom;Sarepta Therapeutics, Inc.Completed10 Years17 YearsMale7Phase 1/Phase 2United Kingdom