Vyondys 53 ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
113筋ジストロフィー1

113. 筋ジストロフィー


臨床試験数 : 622 薬物数 : 485 - (DrugBank : 99) / 標的遺伝子数 : 59 - 標的パスウェイ数 : 168
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT04708314
(ClinicalTrials.gov)
October 31, 202021/9/2020An Open-Label Study of Golodirsen in Non-Ambulant Patients With Duchenne Muscular DystrophyAn Open-Label Study to Evaluate the Safety of Golodirsen in Non-Ambulant Patients With Duchenne Muscular DystrophyDuchenne Muscular DystrophyDrug: Golodirsen 50 MG/1 ML Intravenous Solution [VYONDYS 53]Rare Disease Research, LLCSarepta Therapeutics, Inc.Terminated7 YearsN/AMale2Phase 4United States