Active BMN 111: Daily subcutaneous injection of 15 ug/kg of BMN 111 ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
276軟骨無形成症1

276. 軟骨無形成症


臨床試験数 : 46 薬物数 : 29 - (DrugBank : 6) / 標的遺伝子数 : 5 - 標的パスウェイ数 : 30
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT03989947
(ClinicalTrials.gov)
June 12, 201922/5/2019An Extension Study to Evaluate Safety and Efficacy of BMN 111 in Children With AchondroplasiaA Phase 2 Open-Label Long-Term Extension Study to Evaluate the Safety and Efficacy of BMN 111 in Children With AchondroplasiaAchondroplasiaDrug: Active BMN 111: Daily subcutaneous injection of 15 ug/kg of BMN 111BioMarin PharmaceuticalNULLEnrolling by invitation15 MonthsN/AAll70Phase 2United States;Australia;Japan;United Kingdom