MND-ADA Transduction of CD34+ Cells From Children With ADA-SCID
MND-ADA Transduction of CD34+ Cells From the Bone Marrow Of Children With Adenosine Deaminase (ADA)-Deficient Severe Combined Immunodeficiency (SCID): Effect of Discontinuation of PEG-ADA and Marrow Cytoreduction With Busulfan MND-ADA Transduction of CD34+ Cells From the Bone Marrow Of Children With Adenosine Deaminase (ADA)- ...
Severe Combined Immunodeficiency
Biological: ADA gene transfer
Donald B. Kohn, M.D.
FDA Office of Orphan Products Development;National Institutes of Health (NIH)