Lentiviral G1XCGD Gene Therapy ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
65原発性免疫不全症候群1

65. 原発性免疫不全症候群


臨床試験数 : 482 薬物数 : 653 - (DrugBank : 119) / 標的遺伝子数 : 92 - 標的パスウェイ数 : 212
No.TrialIDDate_
enrollment
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registration
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sponsor
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sponsor
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agemin
Inclusion_
agemax
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gender
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size
PhaseCountries
1NCT02234934
(ClinicalTrials.gov)
October 29, 20154/9/2014Study of Gene Therapy Using a Lentiviral Vector to Treat X-linked Chronic Granulomatous DiseaseA Two-Part, Phase I/II, Non Randomized, Multicenter, Open-Label Study of G1XCGD (Lentiviral Vector Transduced CD34+ Cells) in Patients With X-Linked Chronic Granulomatous DiseaseGranulomatous Disease, Chronic, X-linkedBiological: Lentiviral G1XCGD Gene TherapyUniversity of California, Los AngelesBoston Children's Hospital;National Heart, Lung, and Blood Institute (NHLBI);Genethon;California Institute for Regenerative Medicine (CIRM)Recruiting23 MonthsN/AMale16Phase 1/Phase 2United States