AAV2/5-hPDE6B ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
90網膜色素変性症1

90. 網膜色素変性症


臨床試験数 : 130 薬物数 : 180 - (DrugBank : 41) / 標的遺伝子数 : 49 - 標的パスウェイ数 : 109
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT03328130
(ClinicalTrials.gov)
November 6, 20175/10/2017Safety and Efficacy Study in Patients With Retinitis Pigmentosa Due to Mutations in PDE6B GeneSafety and Efficacy of a Unilateral Subretinal Administration of HORA-PDE6B in Patients With Retinitis Pigmentosa Harbouring Mutations in the PDE6B Gene Leading to a Defect in PDE6ß ExpressionRetinitis PigmentosaBiological: AAV2/5-hPDE6BCoave TherapeuticsNULLActive, not recruiting18 YearsN/AAll17Phase 1/Phase 2France