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 244. Maple syrup urine disease
 [ 1 clinical trial,    1 drug(DrugBank: 1 drug),    0 target gene / 0 target pathway

Searched query = "Maple syrup urine disease", "MSUD"
The queries were searched in Public_title, Scientific_title, and Condition of the data. Export date: 11/20/2019. Trials are sorted by Date_enrolment from most recent to oldest in the table.

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1NCT01529060February 201318 March 2019Phenylbutyrate Therapy for Maple Syrup Urine DiseaseA Double-Blind, Randomized, Placebo-Controlled, Crossover Trial of Phenylbutyrate in the Treatment of Maple Syrup Urine DiseaseMaple Syrup Urine DiseaseDrug: Phenylbutyrate;Drug: Placebo powderBrendan LeeNot recruiting3 YearsN/AAll20Phase 2/Phase 3United States