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KEGG GENES
KEGG PATHWAY
KEGG DRUG
DrugBank
指定難病告示番号
1
SMN1
💬
1.
SMN1
×
Name
Full Name
SMN1
survival of motor neuron 1, telomeric
-
Onasemnogene abeparvovec
Onasemnogene abeparvovec
💬
1.
SMN1
×
Name
Other Names
Onasemnogene abeparvovec
Onasemnogene abeparvovec (USAN/INN)
Onasemnogene abeparvovec-xioi
Zolgensma (TN)
オナセムノゲンアベパルボベク
ゾルゲンスマ
Onasemnogene abeparvovec
1件:
3
3
💬
1.
SMN1
×
告示番号
日本語名
英語名
3
脊髄性筋萎縮症
Spinal muscular atrophy