NPC-09

( DrugBank: - / KEGG DRUG: - )

1 disease

告示番号	疾患名（ページ内リンク）	臨床試験数
30	遠位型ミオパチー	5

30. 遠位型ミオパチー

臨床試験数 : 15 / 薬物数 : 17 - (DrugBank : 3) / 標的遺伝子数 : 1 - 標的パスウェイ数 : 1

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Showing 1 to 5 of 5 trials

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	JPRN-jRCT2021200030 (jRCT2021200030)	08/02/2021	07/12/2020	Efficacy confirmation study of NPC-09	Efficacy confirmation study of NPC-09 - NPC-09-1	Distal myopathy with rimmed vacuoles (DMRV), hereditary inclusion body myopathy (hIBM)	Oral administration of NPC-09 (Aceneuramic acid) for 48 weeks as compared with placebo	Suzuki Ryoichi	NULL	Not Recruiting	>= 20age old	<= 50age old	Both	10	Phase 3	Japan
2	NCT04671472 (ClinicalTrials.gov)	February 8, 2021	30/11/2020	Efficacy Confirmation Study of NPC-09	Efficacy Confirmation Study of NPC-09	GNE Myopathy;Distal Myopathy With Rimmed Vacuoles (DMRV);Hereditary Inclusion Body Myopathy (hIBM);N ...	Drug: NPC-09;Drug: NPC-09 placebo	Nobelpharma	NULL	Completed	20 Years	50 Years	All	14	Phase 3	Japan
3	JPRN-UMIN000026354	2017/03/28	20/03/2017	A Phase II/III Open-label Extension Study of NPC-09(N-acetylneuraminic acid) in Patients with GNE My ...	A Phase II/III Open-label Extension Study of NPC-09(N-acetylneuraminic acid) in Patients with GNE My ...	GNE myopathy (Distal myopathy with rimmed vacuoles (DMRV), hereditary inclusion body myopathy (hIBM) ...	SA-ER 2g 3 times oral dosing a day for 48 consecutive weeks	Tohoku University Hospital, Department of Neurology	Nobelpharma Co., Ltd.	Complete: follow-up complete	20years-old	50years-old	Male and Female	20	Phase 2,3	Japan
4	JPRN-UMIN000020683	2016/02/01	25/01/2016	A Phase II/III Study of NPC-09 (N-acetylneuraminic acid) in Patients with GNE Myopathy (GNEM)	A Phase II/III Study of NPC-09(N-acetylneuraminic acid) in Patients with GNE Myopathy (GNEM) - A Pha ...	GNE myopathy (Distal myopathy with rimmed vacuoles (DMRV), hereditary inclusion body myopathy (hIBM) ...	SA-ER 2g 3 times oral dosing a day for 48 consecutive weeks placebo 3 times oral dosing a day for 48 ...	Tohoku University Hospital, Department of Neurology	Nobelpharma Co., Ltd.	Complete: follow-up complete	20years-old	50years-old	Male and Female	20	Phase 2,3	Japan
5	NCT01236898 (ClinicalTrials.gov)	November 2010	8/11/2010	Pharmacokinetic Study on N-acetylneuraminic Acid	Pharmacokinetic Study on N-acetylneuraminic Acid in Patients With Distal Myopathy With Rimmed Vacuol ...	Nonaka Myopathy;Hereditary Inclusion Body Myopathy	Drug: NPC-09	Tohoku University	NULL	Completed	20 Years	40 Years	Both	6	Phase 1	Japan

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