113. 筋ジストロフィー Muscular dystrophy Clinical trials / Disease details


臨床試験数 : 646 薬物数 : 471 - (DrugBank : 105) / 標的遺伝子数 : 59 - 標的パスウェイ数 : 170

  
1 trial found
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1NCT00159250
(ClinicalTrials.gov)
October 26, 20078/9/2005Safety and Efficacy Study of Antisense Oligonucleotides in Duchenne Muscular DystrophyRestoring Dystrophin Expression in Duchenne Muscular Dystrophy: A Phase I/II Clinical Trial Using AVI-4658Duchenne Muscular DystrophyDrug: AVI-4658 (PMO)Imperial College LondonDepartment of Health, United Kingdom;Sarepta Therapeutics, Inc.Completed10 Years17 YearsMale7Phase 1/Phase 2United Kingdom