113. 筋ジストロフィー Muscular dystrophy Clinical trials / Disease details


臨床試験数 : 646 薬物数 : 471 - (DrugBank : 105) / 標的遺伝子数 : 59 - 標的パスウェイ数 : 170

  
1 trial found
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1NCT00844597
(ClinicalTrials.gov)
January 200924/12/2008Dose-Ranging Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy (DMD) PatientsClinical Study to Assess the Safety fo AVI-4658 in Subjects With Duchenne Muscular Dystrophy Due to a Frame-shift Mutation Amenable to Correction by Skipping Exon 51.Duchenne Muscular DystrophyDrug: AVI-4658 for InjectionSarepta TherapeuticsBritish Medical Research CouncilCompleted5 Years15 YearsMale19Phase 1/Phase 2United Kingdom