140. ドラベ症候群 Dorabe syndrome Clinical trials / Disease details


臨床試験数 : 116 薬物数 : 65 - (DrugBank : 17) / 標的遺伝子数 : 50 - 標的パスウェイ数 : 64

  
1 trial found
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agemin
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1NCT02758626
(ClinicalTrials.gov)
November 20164/4/2016Ataluren for Nonsense Mutation in CDKL5 and Dravet SyndromeA Phase 2 Randomized, Double-Masked Placebo-Controlled Crossover Safety and Tolerability Study of Ataluren for Drug Resistant Epilepsy in Patients With Nonsense Mutation CDKL5 or Dravet SyndromeEpilepsyDrug: ataluren;Drug: PlaceboNYU Langone HealthPTC TherapeuticsCompleted2 Years12 YearsAll16Phase 2United States