169. メンケス病 Menkes disease Clinical trials / Disease details


臨床試験数 : 6 薬物数 : 6 - (DrugBank : 4) / 標的遺伝子数 : 9 - 標的パスウェイ数 : 14

  
1 trial found
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1NCT04977388
(ClinicalTrials.gov)
July 12, 20219/7/2021NORTHERA (DROXIDOPA) for Dysautonomia in Adult Survivors of Menkes Disease and Occipital Horn SyndromePhase I/II Study of NORTHERA (DROXIDOPA) for Dysautonomia in Adult Survivors of Menkes Disease and Adults With Occipital Horn Syndrome: Double-blind Placebo-controlled Randomized Crossover Clinical TrialMenkes Disease;Occipital Horn SyndromeDrug: Droxidopa;Other: PlaceboStephen G. Kaler, MDNULLRecruiting18 Years50 YearsAll6Phase 1/Phase 2United States