20. 副腎白質ジストロフィー Adrenoleukodystrophy Clinical trials / Disease details


臨床試験数 : 61 薬物数 : 90 - (DrugBank : 31) / 標的遺伝子数 : 23 - 標的パスウェイ数 : 126

  
1 trial found
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT02204904
(ClinicalTrials.gov)
April 201528/7/2014Observational Study to Evaluate Allogeneic HSCT Outcomes for Cerebral Adrenoleukodystrophy (CALD)A Prospective and Retrospective Data Collection Study to Evaluate Outcomes in Males =17 Years of Age Undergoing Allogeneic Hematopoietic Stem Cell Transplantation for the Treatment of Cerebral AdrenoleukodystrophyX-Linked Adrenoleukodystrophy (X-ALD);Cerebral Adrenoleukodystrophy (CALD);Adrenoleukodystrophy (ALD)Genetic: Allo-HSCTbluebird bioNULLTerminatedN/A17 YearsMale59United States;Argentina;Canada;Germany;Italy;Netherlands;United Kingdom