DDrare
Disease
Drug
Target Gene/Pathway
問合せ先
EN
20. 副腎白質ジストロフィー
Adrenoleukodystrophy
Clinical trials
/
Disease details
臨床試験数
:
61
/
薬物数
:
90
- (
DrugBank
:
31
) /
標的遺伝子数
:
23
-
標的パスウェイ数
:
126
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No.
TrialID
Date_
enrollment
Date_
registration
Public_title
Scientific_title
Condition
Intervention
Primary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
Phase
Countries
1
NCT00176904
(
ClinicalTrials.gov
)
January 1995
12/9/2005
Stem Cell Transplant for Inborn Errors of Metabolism
Treatment of Lysosomal and Peroxisomal Inborn Errors of Metabolism by Bone Marrow Transplantation
Adrenoleukodystrophy;Metachromatic Leukodystrophy;Globoid Cell Leukodystrophy;Gaucher's Disease;Fucosidosis;Wolman Disease;Niemann-Pick Disease;Batten Disease;GM1 Gangliosidosis;Tay Sachs Disease;Sandhoff Disease
Adrenoleukodystrophy;Metachromatic Leukodystrophy;Globoid Cell Leukodystrophy;Gaucher's Disease;Fuco ...
Procedure: Stem Cell Transplant;Drug:
Busulfan
, Cyclophosphamide, Antithymocyte Globulin
Masonic Cancer Center, University of Minnesota
NULL
Completed
N/A
N/A
All
135
Phase 2/Phase 3
United States