DDrare
Disease
Drug
Target Gene/Pathway
問合せ先
EN
20. 副腎白質ジストロフィー
Adrenoleukodystrophy
Clinical trials
/
Disease details
臨床試験数
:
61
/
薬物数
:
90
- (
DrugBank
:
31
) /
標的遺伝子数
:
23
-
標的パスウェイ数
:
126
Search
2 trials found
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No.
TrialID
Date_
enrollment
Date_
registration
Public_title
Scientific_title
Condition
Intervention
Primary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
Phase
Countries
1
NCT02961803
(
ClinicalTrials.gov
)
October 2014
9/11/2016
MD1003
-AMN
MD1003
in Adrenomyeloneuropathy
MD1003
in Adrenomyeloneuropathy : a Randomized Double Blind Placebo Controlled Study
Adrenomyeloneuropathy;Adrenoleukodystrophy;AMN
Drug:
MD1003
100 mg capsule
;Drug: Placebo
MedDay Pharmaceuticals SA
NULL
Completed
18 Years
60 Years
Male
67
Phase 2/Phase 3
France;Germany;Spain
2
EUCTR2014-000698-38-ES
(
EUCTR
)
13/08/2014
13/06/2014
MD1003
IN ADRENOMYELONEUROPATHY
MD1003
IN ADRENOMYELONEUROPATHY: A RANDOMIZED DOUBLE BLIND PLACEBO CONTROLLED STUDY -
MD1003
-AMN
Adrenomyeloneuropathy
MedDRA version: 17.0;Level: LLT;Classification code 10069075;Term: Adrenomyeloneuropathy without cerebral involvement;System Organ Class: 100000004850;Therapeutic area: Diseases [C] - Nervous System Diseases [C10]
Adrenomyeloneuropathy
MedDRA version: 17.0;Level: LLT;Classification code 10069075;Term: Adrenomyelo ...
Product Name:
biotin
Product Code:
MD1003
INN or Proposed INN:
D-BIOTIN
MEDDAY SAS
NULL
Not Recruiting
Female: no
Male: yes
60
Phase 2;Phase 3
Spain