DDrare
Disease
Drug
Target Gene/Pathway
問合せ先
EN
20. 副腎白質ジストロフィー
Adrenoleukodystrophy
Clinical trials
/
Disease details
臨床試験数
:
61
/
薬物数
:
90
- (
DrugBank
:
31
) /
標的遺伝子数
:
23
-
標的パスウェイ数
:
126
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No.
TrialID
Date_
enrollment
Date_
registration
Public_title
Scientific_title
Condition
Intervention
Primary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
Phase
Countries
1
NCT00383448
(
ClinicalTrials.gov
)
September 2006
29/9/2006
HSCT for High Risk Inherited Inborn Errors
Treatment of High Risk, Inherited Lysosomal And Peroxisomal Disorders by Reduced Intensity Hematopoietic Stem Cell Transplantation
Treatment of High Risk, Inherited Lysosomal And Peroxisomal Disorders by Reduced Intensity Hematopoi ...
Adrenoleukodystrophy;Metachromatic Leukodystrophy;Globoid Cell Leukodystrophy;Tay Sachs Disease;Sandhoffs Disease;Wolman Disease;I-Cell Disease;Sanfilippo Syndrome;GM1 Gangliosidosis
Adrenoleukodystrophy;Metachromatic Leukodystrophy;Globoid Cell Leukodystrophy;Tay Sachs Disease;Sand ...
Drug:
Clofarabine
;Procedure: Total body Irradiation;Drug:
Melphalan
;Biological:
Hematopoietic Stem Cell Transplantation
;Drug:
Alemtuzumab
;Drug:
mycophenylate mofetil
;Device: Cyclosporine A;Drug:
Hydroxyurea
Drug:
Clofarabine
;Procedure: Total body Irradiation;Drug:
Melphalan
;Biological:
Hematopoietic Stem C
...
Masonic Cancer Center, University of Minnesota
NULL
Completed
N/A
70 Years
All
38
Phase 2
United States