20. 副腎白質ジストロフィー Adrenoleukodystrophy Clinical trials / Disease details


臨床試験数 : 61 薬物数 : 90 - (DrugBank : 31) / 標的遺伝子数 : 23 - 標的パスウェイ数 : 126

  
1 trial found
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1NCT05394064
(ClinicalTrials.gov)
June 30, 202216/5/2022A Study to Evaluate Administration of SBT101 Gene Therapy in Adult Patients With Adrenomyeloneuropathy (AMN)A Phase 1/2 Randomized, Blinded, Dose-escalation Study to Evaluate the Safety and Efficacy of Intrathecal Administration of AAV9-ABCD1 Gene Therapy (SBT101) in Adult Patients With AdrenomyeloneuropathyAMN;AMN Gene Mutation;X-ALDGenetic: SBT101;Procedure: Imitation ProcedureSwanBio Therapeutics, Inc.NULLRecruiting18 Years65 YearsMale16Phase 1/Phase 2United States