201. アンジェルマン症候群 Angelman syndrome Clinical trials / Disease details

臨床試験数 : 25 / 薬物数 : 40 - (DrugBank : 11) / 標的遺伝子数 : 22 - 標的パスウェイ数 : 20

1 trial found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT04259281 (ClinicalTrials.gov)	February 24, 2020	31/1/2020	A Study of the Safety and Tolerability of GTX-102 in Children With Angelman Syndrome	A Phase 1/2 Open-label, Multiple-dose, Dose-escalating Clinical Trial of the Safety and Tolerability ...	Angelman Syndrome	Drug: GTX-102	Ultragenyx Pharmaceutical Inc	NULL	Recruiting	4 Years	17 Years	All	83	Phase 1/Phase 2	United States;Canada;United Kingdom

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