201. アンジェルマン症候群 Angelman syndrome Clinical trials / Disease details


臨床試験数 : 25 薬物数 : 40 - (DrugBank : 11) / 標的遺伝子数 : 22 - 標的パスウェイ数 : 20

  
1 trial found
No.TrialIDDate_
enrollment
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registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
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sponsor
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Inclusion_
agemin
Inclusion_
agemax
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gender
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size
PhaseCountries
1NCT05127226
(ClinicalTrials.gov)
December 22, 20219/11/2021HALOS: A Safety, Tolerability, Pharmacokinetics and Pharmacodynamics Study of Multiple Ascending Doses of ION582 in Participants With Angelman SyndromeHALOS: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Intrathecally Administered ION582 in Patients With Angelman SyndromeAngelman SyndromeDrug: ION582Ionis Pharmaceuticals, Inc.BiogenRecruiting2 Years50 YearsAll44Phase 1/Phase 2United States;Australia;Israel;United Kingdom