246. メチルマロン酸血症 Methylmalonic acidemia Clinical trials / Disease details

臨床試験数 : 23 / 薬物数 : 31 - (DrugBank : 8) / 標的遺伝子数 : 17 - 標的パスウェイ数 : 23

2 trials found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	EUCTR2019-001061-32-GB (EUCTR)	25/10/2019	30/05/2019	A clinical study to evaluate mRNA-3704 in Patients with MMA	A Global, Phase 1/2, Open Label, Dose Escalation Study to Evaluate the Safety, Pharmacodynamics, and ...	Isolated Methylmalonic Acidemia Due to Methylmalonyl-CoA Mutase Deficiency;Therapeutic area: Body pr ...	Product Name: mRNA-3704 INN or Proposed INN: NA Other descriptive name: NA	ModernaTX, Inc.	NULL	Not Recruiting			Female: yes Male: yes	34	Phase 1;Phase 2	United States;United Kingdom
2	NCT03810690 (ClinicalTrials.gov)	May 28, 2019	14/1/2019	Open Label Study of mRNA-3704 in Patients With Isolated Methylmalonic Acidemia	A Global, Phase 1/2, Open Label, Dose Escalation Study to Evaluate the Safety, Pharmacodynamics, and ...	Methylmalonic Acidemia (MMA);Metabolism, Inborn Errors	Biological: mRNA-3704	ModernaTX, Inc.	NULL	Withdrawn	1 Year	N/A	All	0	Phase 1/Phase 2	United States

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