299. 嚢胞性線維症 Cystic fibrosis Clinical trials / Disease details


臨床試験数 : 1,695 薬物数 : 1,527 - (DrugBank : 268) / 標的遺伝子数 : 111 - 標的パスウェイ数 : 174

  
1 trial found
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1NCT04732910
(ClinicalTrials.gov)
July 1, 201825/1/2021Cystic Fibrosis Transmembrane Regulator (CFTR) Biomarker Study to Evaluate the Rescue of Mutant CFTR in Patients With Cystic Fibrosis Treated With CFTR-modulatorsCFTR Biomarker Studie Bei Patient*Innen Mit Mukoviszidose Und CFTR-ModulatortherapieCystic FibrosisDrug: Treatment with cystic fibrosis transmembrane regulator (CFTR) modualtors Ivacaftor, Lumacaftor-Ivacaftor, Tezacaftor-Ivacaftor, Elexacaftor-Tezacaftor-IvacaftorCharite University, Berlin, GermanyHannover Medical School;Heidelberg University;University of GiessenRecruiting6 MonthsN/AAll90Germany