299. 嚢胞性線維症 Cystic fibrosis Clinical trials / Disease details


臨床試験数 : 1,695 薬物数 : 1,527 - (DrugBank : 268) / 標的遺伝子数 : 111 - 標的パスウェイ数 : 174

  
1 trial found
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1NCT05668741
(ClinicalTrials.gov)
February 27, 202319/12/2022A Phase 1 Study of VX-522 in Participants With Cystic Fibrosis (CF)A Phase 1 Single Dose Escalation Study Evaluating the Safety and Tolerability of VX-522 in Subjects 18 Years of Age and Older With Cystic Fibrosis and a CFTR Genotype Not Responsive to CFTR Modulator TherapyCystic FibrosisDrug: VX-522 mRNA therapyVertex Pharmaceuticals IncorporatedNULLRecruiting18 Years65 YearsAll9Phase 1United States