113. Muscular dystrophy Clinical trials / Disease details

Clinical trials : 646 / Drugs : 471 - (DrugBank : 105) / Drug target genes : 59 - Drug target pathways : 170

11 trials found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	EUCTR2014-005296-81-BE (EUCTR)	02/05/2016	19/11/2015	A clinical study to provide drisapersen(study medication) to patients withDuchenne disease (muscular ...	A 24 week Randomized Double-Blind, Placebo-Controlled Study followed by 72 week open-label extension ...	Duchenne Muscular Dystrophy (DMD) MedDRA version: 18.1;Level: PT;Classification code 10013801;Term: ...	Product Name: Drisapersen Product Code: Drisapersen INN or Proposed INN: Drisapersen Other descriptive ...	BioMarin Pharmaceutical Inc.	NULL	Not Recruiting			Female: no Male: yes	104	Phase 3	United States;Spain;Turkey;Russian Federation;Israel;United Kingdom;Italy;France;Czech Republic;Cana ...
2	EUCTR2015-001955-54-DE (EUCTR)	13/01/2016	18/08/2015	A clinical study to provide drisapersen(study medication) to patients with Duchenne disease (muscula ...	An open-label extension study of the long-term safety, tolerability and efficacy of drisapersenin su ...	Duchenne Muscular Dystrophy (DMD) MedDRA version: 18.1;Level: PT;Classification code 10013801;Term: ...	Product Name: Drisapersen Product Code: Drisapersen INN or Proposed INN: drisapersen Other descriptive ...	BioMarin Pharmaceutical Inc.	NULL	Not Recruiting			Female: no Male: yes	220	Phase 3	Portugal;Belarus;United States;Taiwan;Spain;Ukraine;Russian Federation;Chile;Israel;Switzerland;Ital ...
3	EUCTR2015-001955-54-BE (EUCTR)	06/01/2016	21/09/2015	A clinical study to provide drisapersen(study medication) to patients with Duchenne disease (muscula ...	An open-label extension study of the long-term safety, tolerability and efficacy of drisapersenin su ...	Duchenne Muscular Dystrophy (DMD) MedDRA version: 18.0;Level: PT;Classification code 10013801;Term: ...	Product Name: Drisapersen Product Code: Drisapersen INN or Proposed INN: drisapersen Other descriptive ...	BioMarin Pharmaceutical Inc.	NULL	Not Recruiting			Female: no Male: yes	220	Phase 3	Portugal;Belarus;United States;Taiwan;Spain;Ukraine;Russian Federation;Chile;Israel;Switzerland;Ital ...
4	EUCTR2015-001955-54-NL (EUCTR)	08/12/2015	09/07/2015	A clinical study to provide drisapersen(study medication) to patients with Duchenne disease (muscula ...	An open-label extension study of the long-term safety, tolerability and efficacy of drisapersenin su ...	Duchenne Muscular Dystrophy (DMD) MedDRA version: 18.0;Level: PT;Classification code 10013801;Term: ...	Product Name: Drisapersen Product Code: Drisapersen	BioMarin Nederland BV	NULL	Not Recruiting			Female: no Male: yes	220	Phase 3	Portugal;United States;Belarus;Taiwan;Spain;Ukraine;Russian Federation;Chile;Israel;Switzerland;Ital ...
5	NCT02636686 (ClinicalTrials.gov)	November 27, 2015	9/12/2015	Extension Study of Drisapersen in DMD Subjects	An Open-label Extension Study of the Long-term Safety, Tolerability and Efficacy of Drisapersenin Su ...	Duchenne Muscular Dystrophy	Drug: Drisapersen	BioMarin Pharmaceutical	NULL	No longer available	5 Years	80 Years	Male			United States;Argentina;Australia;Belgium;Bulgaria;Czechia;France;Germany;Israel;Italy;Japan;Korea, ...
6	EUCTR2015-001955-54-ES (EUCTR)	24/11/2015	05/10/2015	A clinical study to provide drisapersen(study medication) to patients with Duchenne disease (muscula ...	An open-label extension study of the long-term safety, tolerability and efficacy of drisapersenin su ...	Duchenne Muscular Dystrophy (DMD) MedDRA version: 18.0;Level: PT;Classification code 10013801;Term: ...	Product Name: Drisapersen Product Code: Drisapersen INN or Proposed INN: drisapersen Other descriptive ...	BioMarin Pharmaceutical Inc.	NULL	Not Recruiting			Female: no Male: yes	220	Phase 3	United States;Belarus;Portugal;Taiwan;Spain;Ukraine;Chile;Israel;Russian Federation;Italy;Switzerlan ...
7	NCT01890798 (ClinicalTrials.gov)	January 2014	27/6/2013	Drisapersen Duchenne Muscular Dystrophy (DMD) Treatment Protocol	A Continued Access Protocol for Eligible US Subjects With Duchenne Muscular Dystrophy Who Previously ...	Muscular Dystrophies	Drug: Drisapersen	GlaxoSmithKline	NULL	Withdrawn	5 Years	N/A	Male	0	Phase 3	NULL
8	NCT01803412 (ClinicalTrials.gov)	May 1, 2013	28/2/2013	A Study of the Safety, Tolerability & Efficacy of Long-term Administration of Drisapersenin US & Can ...	An Open-label Extension Study of the Long-term Safety, Tolerability and Efficacy of Drisapersenin US ...	Muscular Dystrophies	Drug: Drisapersen	BioMarin Pharmaceutical	NULL	Terminated	5 Years	N/A	Male	53	Phase 3	United States;Canada
9	EUCTR2007-004819-54-SE (EUCTR)	19/03/2008	31/01/2008	A study to assess the effect and safety of multiple subcutaneous doses of drisapersenin patients wit ...	A phase I/II, open label, escalating dose, pilot study to assess the effect, safety, tolerability an ...	Duchenne Muscular Dystrophy MedDRA version: 17.0;Level: PT;Classification code 10013801;Term: Duchen ...	Product Name: Drisapersen Product Code: PRO051 INN or Proposed INN: PRO051 Product Name: Drisapersen Pro ...	Prosensa Therapeutics BV	NULL	Not Recruiting			Female: no Male: yes	12	Phase 1;Phase 2	Belgium;Netherlands;Sweden
10	NCT01910649 (ClinicalTrials.gov)	March 2008	2/8/2012	A Phase I/II, Open Label, Escalating Dose, Pilot Study to Assess Effect, Safety, Tolerability and PK ...	A Phase I/II, Open Label, Escalating Dose, Pilot Study to Assess the Effect, Safety, Tolerability an ...	Muscular Dystrophies	Drug: Drisapersen	BioMarin Pharmaceutical	NULL	Terminated	5 Years	16 Years	Male	12	Phase 2	NULL

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