113. Muscular dystrophy Clinical trials / Disease details


Clinical trials : 646 Drugs : 471 - (DrugBank : 105) / Drug target genes : 59 - Drug target pathways : 170

  
1 trial found
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agemin
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1NCT02354781
(ClinicalTrials.gov)
January 201526/1/2015Clinical Intramuscular Gene Transfer of rAAV1.CMV.huFollistatin344 Trial to Patients With Duchenne Muscular DystrophyPhase I/II Clinical Intramuscular Gene Transfer of rAAV1.CMV.huFollistatin344 Trial to Patients With Duchenne Muscular DystrophyDuchenne Muscular DystrophyBiological: rAAV1.CMV.huFollistin344Jerry R. MendellDuchenne Alliance;Milo TherapeuticsCompleted7 YearsN/AMale3Phase 1/Phase 2United States