113. Muscular dystrophy Clinical trials / Disease details


Clinical trials : 646 Drugs : 471 - (DrugBank : 105) / Drug target genes : 59 - Drug target pathways : 170

  
1 trial found
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1NCT02704325
(ClinicalTrials.gov)
April 201623/12/2015Gene Transfer Clinical Trial for Duchenne Muscular Dystrophy Using rAAVrh74.MCK.GALGT2Phase I Gene Transfer Clinical Trial for Duchenne Muscular Dystrophy Using rAAVrh74.MCK.GALGT2Duchenne Muscular DystrophyBiological: rAAVrh74.MCK.GALGT2;Other: PLACEBO (Saline)Kevin FlaniganNULLWithdrawn9 YearsN/AMale0Phase 1/Phase 2United States