113. Muscular dystrophy Clinical trials / Disease details


Clinical trials : 646 Drugs : 471 - (DrugBank : 105) / Drug target genes : 59 - Drug target pathways : 170

  
1 trial found
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1NCT01976091
(ClinicalTrials.gov)
February 1, 201524/7/2013A Gene Transfer Therapy Study to Evaluate the Safety of SRP-9004 in Participants With Limb-Girdle Muscular Dystrophy, Type 2D (LGMD2D)Phase I/IIA Gene Transfer Clinical Trial for LGMD2D (Alpha-Sarcoglycan Deficiency) Using scAAVrh74.tMCK.hSGCALimb-Girdle Muscular Dystrophy, Type 2DGenetic: SRP-9004Sarepta Therapeutics, Inc.Nationwide Children's HospitalCompleted7 YearsN/AAll6Phase 1/Phase 2United States