A study to investigate the safety, tolerability, and efficacy of SGT-001 in male adolescents and children with Duchenne muscular dystrophy A study to investigate the safety, tolerability, and efficacy of SGT-001 in male adolescents and chi ...
A randomized, controlled, open-label, single-ascending dose, phase I/II study to investigate the safety and tolerability, and efficacy of intravenous SGT-001 in male adolescents and children with Duchenne muscular dystrophy A randomized, controlled, open-label, single-ascending dose, phase I/II study to investigate the saf ...
Product Name: SGT-001 Product Code: rAAV9-CK8-h-µD5 INN or Proposed INN: SGT-001 Other descriptive name: rAAV9-CK8-h-µD5Product Name: SGT-001 Product Code: rAAV9-CK8-h-µD5 INN or Proposed INN: SGT-001 Other descriptive name ...
Solid Biosciences Inc.
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Authorised-recruitment may be ongoing or finished
Female: no Male: yes
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Human pharmacology (Phase 1): yes Therapeutic exploratory (Phase 2): yes Therapeutic confirmatory - (Phase 3): no Therapeutic use (Phase 4): no Human pharmacology (Phase 1): yes Therapeutic exploratory (Phase 2): yes Therapeutic confirmatory - ...