ADVM-043 ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
231α1−アンチトリプシン欠乏症1

231. α1−アンチトリプシン欠乏症


臨床試験数 : 93 薬物数 : 77 - (DrugBank : 8) / 標的遺伝子数 : 10 - 標的パスウェイ数 : 36
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT03804021
(ClinicalTrials.gov)
January 11, 201911/1/2019Long-Term Follow-up Study of ADVM-043Post-treatment Long-term Follow-up Study of ADVM-043 Gene Therapy in Alpha-1 Antitrypsin DeficiencyAlpha-1 Antitrypsin DeficiencyGenetic: ADVM-043Adverum Biotechnologies, Inc.NULLEnrolling by invitation18 YearsN/AAll6United States