RAAV2-CB-hAAT Gene Vector ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
231α1−アンチトリプシン欠乏症1

231. α1−アンチトリプシン欠乏症


臨床試験数 : 93 薬物数 : 77 - (DrugBank : 8) / 標的遺伝子数 : 10 - 標的パスウェイ数 : 36
No.TrialIDDate_
enrollment
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registration
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Inclusion_
agemin
Inclusion_
agemax
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gender
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size
PhaseCountries
1NCT00377416
(ClinicalTrials.gov)
March 200414/9/2006Experimental Gene Transfer Procedure to Treat Alpha 1-Antitrypsin DeficiencyPreclinical & Phase I/II Trials of AAV-AAT Vectors: Phase I Trial of Intramuscular Injection of a Recombinant Adeno-Associated Virus Alpha 1-Antitrypsin (rAAV2-CB-hAAT) Gene Vector to AAT-Deficient AdultsAlpha 1-Antitrypsin DeficiencyGenetic: rAAV2-CB-hAAT Gene VectorUniversity of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI);Alpha-1 Foundation;University of Florida;National Center for Research Resources (NCRR)Completed18 YearsN/AAll12Early Phase 1United States