251. 尿素サイクル異常症 Urea cycle disorder Clinical trials / Disease details

臨床試験数 : 48 / 薬物数 : 52 - (DrugBank : 13) / 標的遺伝子数 : 4 - 標的パスウェイ数 : 29

2 trials found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03181828 (ClinicalTrials.gov)	March 24, 2017	1/6/2017	Manipulating the Gut Microbiome Study	Manipulating the Gut Microbiome Study	Urea Cycle Disorder	Drug: Acetohydroxamic Acid Oral Tablet [Lithostat]	Nicholas Ah Mew	NULL	Terminated	18 Years	60 Years	All	4	Phase 1/Phase 2	United States
2	NCT02670889 (ClinicalTrials.gov)	November 2016	14/1/2016	Urease Inhibitor Drug Treatment for Urea Cycle Disorders	Manipulating the Gut Microbiome in Urea Cycle Disorders	Ornithine Transcarbamylase Deficiency;Argininosuccinate Synthetase Deficiency (Citrullinemia);Argininosuccinic Acid Lyase Deficiency (Argininosuccinic Aciduria);Carbamyl-Phosphate Synthase I Deficiency	Drug: Acetohydroxamic Acid;Drug: Isotopic Intravenous [13C]-Urea	Nicholas Ah Mew	Data Management and Coordinating Center (DMCC);Children's Hospital of Philadelphia	Not yet recruiting	18 Years	60 Years	Both	16	Phase 1/Phase 2	NULL