251. 尿素サイクル異常症 Urea cycle disorder Clinical trials / Disease details
臨床試験数 : 48 / 薬物数 : 52 - (DrugBank : 13) / 標的遺伝子数 : 4 - 標的パスウェイ数 : 29
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT00004386 (ClinicalTrials.gov) | October 1995 | 18/10/1999 | Phase I Pilot Study of Liver-Directed Gene Therapy for Partial Ornithine Transcarbamylase Deficiency | Ornithine Transcarbamylase Deficiency Disease | Genetic: recombinant adenovirus containing the ornithine transcarbamylase gene | Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) | Children's Research Institute | Terminated | 18 Years | 65 Years | Both | Phase 1 | NULL |