251. 尿素サイクル異常症 Urea cycle disorder Clinical trials / Disease details

臨床試験数 : 48 / 薬物数 : 52 - (DrugBank : 13) / 標的遺伝子数 : 4 - 標的パスウェイ数 : 29

1 trial found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03767270 (ClinicalTrials.gov)	December 2019	28/11/2018	Safety, Tolerability and PK/PD Evaluation of Intravenous Administration of MRT5201in Patients With O ...	A Phase 1/2 Single Ascending Dose Study Evaluating the Safety, Tolerability, Pharmacokinetics, and P ...	Ornithine Transcarbamylase Deficiency	Biological: MRT5201;Other: Placebo	Translate Bio, Inc.	NULL	Withdrawn	18 Years	N/A	All	0	Phase 1/Phase 2	NULL

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