Nusinersen Injectable Product ( DrugBank: Nusinersen )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
3脊髄性筋萎縮症1

3. 脊髄性筋萎縮症


臨床試験数 : 217 薬物数 : 149 - (DrugBank : 33) / 標的遺伝子数 : 54 - 標的パスウェイ数 : 80
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT04404764
(ClinicalTrials.gov)
May 27, 202019/5/2020Characterization of the Clinical-epidemiological Profile of Patients With SMA5q Types II and III: Observational StudyCharacterization of the Clinical-epidemiological Profile of Patients With Spinal Muscular Atrophy (SMA) 5q Types II and III in Follow-up in the Brazilian Unified Public Health System: A Cross-sectional Observational Study (Registry)Spinal Muscular AtrophyDrug: Nusinersen Injectable ProductHospital Israelita Albert EinsteinMinistry of Health, BrazilCompleted6 MonthsN/AAll155Brazil