Sodium phenylbutyrate (NaPB) ( DrugBank: Phenylbutyrate )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
3脊髄性筋萎縮症1

3. 脊髄性筋萎縮症


臨床試験数 : 217 薬物数 : 149 - (DrugBank : 33) / 標的遺伝子数 : 54 - 標的パスウェイ数 : 80
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agemin
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PhaseCountries
1NCT00528268
(ClinicalTrials.gov)
July 200710/9/2007Study to Evaluate Sodium Phenylbutyrate in Pre-symptomatic Infants With Spinal Muscular AtrophyProspective Phase I/II Study to Evaluate Effects of Sodium Phenylbutyrate in Pre-symptomatic Infants With Spinal Muscular AtrophySpinal Muscular AtrophyDrug: Sodium phenylbutyrate (NaPB)University of UtahEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)CompletedN/A6 MonthsAll14Phase 1/Phase 2United States