21. ミトコンドリア病 Mitochondrial disease Clinical trials / Disease details


臨床試験数 : 39 薬物数 : 42 - (DrugBank : 32) / 標的遺伝子数 : 47 - 標的パスウェイ数 : 67

  
1 trial found
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1NCT05241262
(ClinicalTrials.gov)
December 1, 20223/2/2022Study of N-acetylcysteine in the Treatment of Patients With the m.3243A>G Mutation and Low Brain Glutathione LevelsA Multiple Ascending Phase 1 Dose Study of N-acetylcysteine in the Treatment of Patients With the m.3243A>G Mutation and Low Brain Glutathione LevelsMitochondrial DiseaseDrug: N-AcetylcysteineDarryl C. De Vivo, MDUnited States Department of DefenseRecruiting18 Years80 YearsAll18Phase 1United States