Pheburane ( DrugBank: - )

---

1 disease

告示番号	疾患名（ページ内リンク）	臨床試験数
21	ミトコンドリア病	1

21. ミトコンドリア病

---

臨床試験数 : 39 /  薬物数 : 42 - (DrugBank : 32) / 標的遺伝子数 : 47 - 標的パスウェイ数 : 67

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	EUCTR2018-001094-25-IT (EUCTR)	12/09/2019	20/05/2021	Clinical trial with Phenilbutirrate to reduce lactic acid in patients affected with Melas Syndrome and PHD deficency encephalopathy	Phenylbutyrate Therapy in Mitochondrial Disease with lactic acidosis: an opel label clinical trial in MELAS and PHD deficiency patients - PHEMI	Melas Syndrome and PDH deficency enchephalopathy MedDRA version: 20.0;Level: PT;Classification code 10053872;Term: MELAS syndrome;System Organ Class: 10010331 - Congenital, familial and genetic disorders MedDRA version: 20.0;Level: LLT;Classification code 10062950;Term: Leigh syndrome;System Organ Class: 10010331 - Congenital, familial and genetic disorders;Therapeutic area: Diseases [C] - Nutritional and Metabolic Diseases [C18]	Trade Name: Feburane Product Name: pheburane Product Code: [A042917017]	FONDAZIONE IRCCS ISTITUTO NEUROLOGICO CARLO BESTA	NULL	Authorised-recruitment may be ongoing or finished			Female: yes Male: yes	9	Phase 2	Italy