EN001 ( DrugBank: - )

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2 diseases

ID	Disease name (Link within this page)	Number of trials
10	Charcot-Marie-Tooth disease	1
113	Muscular dystrophy	1

10. Charcot-Marie-Tooth disease

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Clinical trials : 41 /  Drugs : 46 - (DrugBank : 9) / Drug target genes : 11 - Drug target pathways : 15

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT05333406 (ClinicalTrials.gov)	February 22, 2022	6/1/2022	Determine the Safety and Dose of EN001 in Patients With Charcot-Marie-Tooth Disease (CMT) Type 1A	Open-label, Dose-escalation, Phase 1 Clinical Trial to Determine the Safety and Dose of EN001 in Patients With Charcot-Marie-Tooth Disease (CMT) Type 1A	Charcot-Marie-Tooth Disease, Type IA	Drug: EN001	ENCell	NULL	Completed	19 Years	75 Years	All	9	Phase 1	Korea, Republic of

113. Muscular dystrophy

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Clinical trials : 646 /  Drugs : 471 - (DrugBank : 105) / Drug target genes : 59 - Drug target pathways : 170

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT05338099 (ClinicalTrials.gov)	January 18, 2022	6/1/2022	Determine the Safety and Dose of EN001 in Patients With Duchenne Muscular Dystrophy(DMD)	Open-label, Dose-escalation, Phase 1 Clinical Trial to Determine the Safety and Dose of EN001 in Patients With Duchenne Muscular Dystrophy(DMD)	Duchenne Muscular Dystrophy	Drug: EN001	ENCell	NULL	Completed	2 Years	18 Years	Male	7	Phase 1	Korea, Republic of