19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 854 / 薬物数 : 716 - (DrugBank : 105) / 標的遺伝子数 : 70 - 標的パスウェイ数 : 191

2 trials found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT01614431 (ClinicalTrials.gov)	March 2011	19/5/2012	N Acetyl Cysteine for Cystinosis Patients	N Acetyl Cysteine Can Decrease the Progression of Renal Disease in Cystinosis Patients	Renal Disease;Cystinosis	Drug: N acetyl cysteine	University of Sao Paulo	Fundação de Amparo à Pesquisa do Estado de São Paulo	Completed	1 Year	18 Years	Both	23	Phase 4	NULL
2	NCT00975689 (ClinicalTrials.gov)	August 2009	10/9/2009	Biomarker Validation for Niemann-Pick Disease, Type C: Safety and Efficacy of N-Acetyl Cysteine	Biomarker Validation for Niemann-Pick Disease, Type C: Safety and Efficacy of N-Acetyl Cysteine	Niemann-Pick Disease, Type C	Drug: N-Acetyl Cysteine	Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)	University of Oxford;Washington University School of Medicine;National Human Genome Research Institute (NHGRI)	Completed	12 Months	N/A	All	35	Phase 1/Phase 2	United States