4D-310 ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
19ライソゾーム病1

19. ライソゾーム病


臨床試験数 : 854 薬物数 : 716 - (DrugBank : 105) / 標的遺伝子数 : 70 - 標的パスウェイ数 : 191
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT04519749
(ClinicalTrials.gov)
September 1, 202014/8/2020An Open-label, Phase 1/2 Trial of Gene Therapy 4D-310 in Adult Males With Fabry DiseaseAn Open-label, Phase 1/2 Trial of Gene Therapy 4D-310 in Adult Males With Fabry DiseaseFabry DiseaseBiological: 4D-3104D Molecular TherapeuticsNULLRecruiting18 YearsN/AMale18Phase 1/Phase 2United States